A 2016 to 2021 landscape review presents an overall picture of UK rare disease research funding across government, charities and industry.
There are an estimated 3.5 million people in the UK living with a rare disease.
There are over 7,000 rare diseases, with around 95% of these health conditions lacking an effective treatment.
75% of rare diseases affect children and more than 30% of children with a rare disease die before their fifth birthday.
